Gene therapy

Question 1

gene therapy

Answer 1

• technique replacing faulty genes with new genes to cure disease
• allows for the ability to introduce a normal copy of a gene to restore a faulty or missing gene

Question 2

How are genes introduced into the body?

Answer 2

• vectors are used for delivery

- challenges may be overcome by better delivery to genes and new genes precisely controlled by the body

Question 3

direct delivery

Answer 3

• can be injected intravenously (by IV) into specific tissue

Question 4

cell-based delivery

Answer 4

• cells removed and exposed to vector

- returned to patient