ATMPs

Question 1

What are ATMPs?

Answer 1

Innovative therapies that include gene therapies, cell therapies, somatic-cell therapies and tissue-engineered products. ATMPs are designed to treat, prevent, or diagnose diseases and have the potential to provide significant advancements in medical treatment.

Question 2

What is the aim of gene therapy?

Answer 2

Deliver healthy versions of a gene to correct a defect

Question 3

How does gene therapy work? (simple)

Answer 3

Inserting recombinant genes into the body to treat diseases

Question 4

What is the aim of somatic cell therapy?

Answer 4

Cells are manipulated to function differently to how it normally does in a healthy body

Question 5

How does somatic cell therapy work? (simple)

Answer 5

T-cells are taken from a patient and re-engineered to fight a disease (e.g. cancer)

Question 6

What part of the human body can be regenerated and what specifically allows regeneration to occur?

Answer 6

Human liver can be regenerated.

Special epithelial cells on the liver (hepatocytes in zone 2 that lie between the portal + central vein) are responsible.